Pluto Bioinformatics
GSE100943: Microsatellite expansion RNA visualization, elimination, and reversal of molecular pathology by RNA-targeting Cas9
Bulk RNA sequencing
In this Study, we used RNA-targeting Cas9 (RCas9) to reverse characteristic Myotonic Dystrophy (DM1) cellular phenotypes such as elimination of RNA foci, MBNL relocalization, and reversal of transcriptome-wide splicing. SOURCE: Ranjan Batra (ranjanbatra9@yahoo.com) - Yeo Lab University of California San Diego